Here you will find news updates, papers and links from the Clinical Trial Team in Birmingham, USA and other Researchers globally.
UK – Therapeutic Advances in Rare Disease – August 2021
A recently published review from Dr Patrick Yu Wai Man’s team at Cambridge University Hospital.
USA – Trial and Research Updates from Dr Fumi Urano – August 2021
Spain Gene Therapy to get a treatment for Wolfram Syndrome – Spanish WS Association – August 2021
We are proud to announce that, together with researchers from the Autonomous University of Barcelona (UAB), we have started the first gene therapy project for Wolfram Syndrome
UK TREATWolfram Trial Update – Prof Barrett – June 2021
USA Trial and Research Updates from Dr Fumi Urano – May 2021
Acknowledgments also to the White Foundation for their help in referring patients to Dr Urano’s research. They were unfortunately omitted from the blog sent out in the newsletter.
Portugal – Wolfram syndrome: a Portuguese Research – May 2021
USA Psychiatric Diagnoses and Treatment in Wolfram Syndrome
UK TREATWolfram Trial – update from Prof Tim Barrett – February 2021
Estonian Research February 2021 – Liraglutide, 7,8-DHF and their co-treatment prevents loss of vision and cognitive decline in a Wolfram syndrome rat model.
UK TREATWolfram Trial – Adult’s update from Dr Ben Wright – February 2021
Due to continued Coronavirus pressure this year on delivery of adult Queen Elizabeth hospital medical services, we were requested to pause further recruitment to the TreatWolfram study. This was disappointing, but understandable. We remain committed to the safe delivery of this trial, and will seek to re-open recruitment again as soon as permitted to do so. People currently enrolled to the trial will continue to be supported by the trial team. Whilst some members of the trial team have been redeployed to other hospital roles during this time they will continue to respond to any trial questions raised but may take longer to do so. Their contact email is NeurologyResearchTeam@uhb.nhs.uk
USA Trial and Research Updates from Dr Fumi Urano – February 2021
Adult Trial Recruitment Webinar – 9th November 2020
Virtual Tour of I-Stem Research Labs, France – October 2020.
For those interested in research you might like to watch this short video from the I-Stem Research Centre in France.
I-Stem is the largest French laboratory for research and development dedicated to human pluripotent stem cells, of embryonic origin or obtained by reprogramming gene. https://www.istem.eu/en/
The video has subtitles for the researchers speaking in French, so apologies to those who are VI.
USA Trial Update from Dr Fumi Urano – September 2020
TREATWolframTrial Update from Prof Tim Barrett – September 2020
Wolfram Syndrome Treatment Pipeline – Updated September 2020
Click image for full view.
Two new red bars added.
Wolfram Syndrome Treatment Pipeline – Updated August 2020
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TREATWolfram Update from Prof Barrett – 15th June 2020
TREATWolfram Adult Recruitment Update from Dr Wright – 12th June 2020
USA update from Dr Fumi Urano – 25th April 2020
An easy read version of the medical research paper below.
USA Research Paper – Diabetes reversed in mice with genetically edited stem cells derived from patients – April 2020
TREATWolfram Trial Update – March 2020
USA Update from Dr Fumi Urano – February 2020
Zebrafish Model Update, UK Research (linked information on 2018 trials page) – February 2020
Wolfram Syndrome Treatment Pipeline – Updated October 2019
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How do faults in the WFS1 gene lead to cell death in Wolfram syndrome? – posted Feb 2020
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